Gene therapies can reduce treatment burden and costs for patients with blood disorders

A new analysis found potential gene therapies for blood disorders like hemophilia, beta thalassemia, and sickle cell disease hold promise in dramatically reducing existing treatment burdens for...
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Rare Disease Day: Unmet need inspires innovation

Today, we celebrate Rare Disease Day to both reflect on the progress made toward conquering rare diseases and recognize the continued unmet medical need for these devastating, complex conditions.
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Record number of personalized medicines approved in 2017

We are in an exciting time in biomedical innovation, as rapid scientific and technological advances are leading to new ways of preventing, diagnosing, and treating disease. Nothing illustrates the...
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More than 240 immuno-oncology treatments in development to fight cancer

The American Cancer Society estimates that in 2017 alone, there will be more than 1.6 million new cases of cancer and 600,000 cancer deaths in the United States. With estimates like these, the need...
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ICYMI: The New Era of Medicine initiative spotlights genomics in NYC

As the understanding of each person’s unique DNA makeup continues to grow (better known as genomics), personalized medicine is rapidly reaching new heights.
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Significant progress fighting cancer: Death rate has dropped 25 percent

Cancers have long been one of the most devastating and complex disease areas facing patients. But thanks in part to innovative advancements in treatments and early detection, the cancer death rate in...
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Building on the promise of personalized medicine

PhRMA’s member companies are on the leading edge of personalized medicine development– an area that is transforming health care, improving patient outcomes and creating health system efficiencies. In
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What they are saying about ICER’s scoping document for non-small cell lung cancer

The Institute for Clinical and Economic Review (ICER) has set its sights on a new target: life-saving treatments for advanced non-small cell lung cancer (NSCLC). ICER’s latest draft scoping document...
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New report: Decade of breakthroughs in cancer

The pace of science is yielding remarkable innovation for cancer patients as we learn more about the underlying factors driving the spread and growth of cancer. These advances are opening new doors...
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We are at a pivotal time in health care in America. Biomedical discovery and innovation have the potential to revolutionize the way we diagnose and treat patients. At the same time, rapidly changing...
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